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Revenue Recognition - Additional Information (Detail) - USD ($)
3 Months Ended 6 Months Ended
Sep. 03, 2014
Jan. 30, 2014
Mar. 31, 2014
Jun. 30, 2016
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Non-refundable up-front payment       $ 2,000,000
Payment to be received upon signing of agreement       125,675
Revenue recognized       2,115,000
Revenue recognized under revenue recognition, up front payment     $ 2,000,000  
Clinical Development        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Milestone Payment       60,000,000
Potential milestone payments to be received       60,000,000
Initial Commercial Sales        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Potential milestone payments to be received       100,000,000
BioMarin Pharmaceutical, Inc. | Asset Purchase Agreement        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Upfront payment received under purchase agreement   $ 2,000,000    
Potential milestone payments to be received       160,000,000
Provision for refund       $ 0
BioMarin Pharmaceutical, Inc. | Clinical Development | Asset Purchase Agreement        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Percentage relate to clinical development from Milestone payment       37.00%
BioMarin Pharmaceutical, Inc. | Initial Commercial Sales | Asset Purchase Agreement        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Percentage relate to clinical development from Milestone payment       63.00%
BioMarin Pharmaceutical, Inc. | Technology Transfer Payments | Asset Purchase Agreement        
Revenue Recognition, Multiple-deliverable Arrangements [Line Items]        
Milestone Payment $ 125,675