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Income Taxes - Deferred tax assets and liabilities (Details) - USD ($)
$ in Thousands
Dec. 31, 2023
Dec. 31, 2022
Deferred tax assets:    
Net operating loss carryforwards $ 153,685 $ 135,470
Research and development credits 16,139 14,380
Orphan drug credit 25,484 19,281
Capitalized license fee 2,311 2,776
Stock-based compensation 13,159 11,074
Section 174 Costs 50,688 29,663
Deferred revenue 350 438
Accrued Expenses & Other 5,680 4,536
Total deferred tax assets 267,496 217,618
Valuation allowance (267,158) (217,257)
Net deferred tax assets 338 361
Deferred tax liabilities:    
Operating lease right-of-use asset and other (338) (361)
Total deferred tax liabilities: $ (338) $ (361)