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Revenue recognition - Net Product Sales (Details)
$ in Thousands
3 Months Ended
Mar. 31, 2022
USD ($)
Distributor
segment
Mar. 31, 2021
USD ($)
Distributor
Dec. 31, 2021
USD ($)
Net product sales      
Number of operating segments | segment 1    
Revenue $ 148,735 $ 117,942  
Number of distributors | Distributor 2 2  
Contract with customer, liability $ 0   $ 0
Performance obligations satisfied in period $ 0 $ 2,100  
Minimum      
Net product sales      
Percentage of net product sales threshold 10.00% 10.00%  
Net product revenue      
Net product sales      
Revenue $ 129,832 $ 91,280  
Net product revenue | Non-US      
Net product sales      
Revenue 81,200 47,800  
Emflaza | United States      
Net product sales      
Revenue 48,600 43,500  
Translarna | Non-US      
Net product sales      
Revenue $ 79,200 $ 46,500