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Revenue recognition - Net Product Sales (Details)
$ in Thousands
3 Months Ended 6 Months Ended
Jun. 30, 2022
USD ($)
Distributor
Jun. 30, 2021
USD ($)
Distributor
Jun. 30, 2022
USD ($)
Distributor
segment
Jun. 30, 2021
USD ($)
Distributor
Dec. 31, 2021
USD ($)
Net product sales          
Number of operating segments | segment     1    
Revenue $ 165,526 $ 116,676 $ 314,262 $ 234,620  
Number of distributors | Distributor 2 2 2 2  
Contract with customer, liability $ 0   $ 0   $ 0
Performance obligations satisfied in period $ 0 $ 1,900 $ 0 $ 4,000  
Minimum          
Net product sales          
Percentage of net product sales threshold 10.00% 10.00% 10.00% 10.00%  
Net product revenue          
Net product sales          
Revenue $ 143,701 $ 103,113 $ 273,534 $ 194,393  
Net product revenue | Non-US          
Net product sales          
Revenue 86,900 54,000 168,100 101,700  
Emflaza | United States          
Net product sales          
Revenue 56,800 49,100 105,400 92,700  
Translarna | Non-US          
Net product sales          
Revenue $ 77,000 $ 52,600 $ 156,200 $ 99,100