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Revenue recognition - Net Product Sales (Details)
$ in Thousands
3 Months Ended 6 Months Ended
Jun. 30, 2023
USD ($)
segment
Distributor
country
Jun. 30, 2022
USD ($)
country
segment
Distributor
Jun. 30, 2023
USD ($)
segment
Distributor
country
Jun. 30, 2022
USD ($)
segment
country
Distributor
Dec. 31, 2022
USD ($)
Revenue recognition          
Number of operating segments | segment 1 1 1 1  
Revenue $ 213,808 $ 165,526 $ 434,190 $ 314,262  
Net product revenue | Geographic concentration risk          
Revenue recognition          
Number of countries exceeding 10% of net product sales | country 3 2 3 3  
Percentage of net product sales threshold 10.00% 10.00% 10.00% 10.00%  
Net product revenue | Geographic concentration risk | United States          
Revenue recognition          
Revenue $ 65,700 $ 56,800 $ 120,300 $ 105,400  
Net product revenue | Geographic concentration risk | Russia          
Revenue recognition          
Revenue 19,100 $ 23,600 63,700 28,900  
Net product revenue | Geographic concentration risk | Brazil          
Revenue recognition          
Revenue $ 23,100   $ 48,900 $ 32,500  
Net product revenue | Customer concentration risk          
Revenue recognition          
Number of distributors | Distributor 2 2 2 2  
Percentage of net product sales threshold 10.00% 10.00% 10.00% 10.00%  
Net product revenue          
Revenue recognition          
Revenue $ 174,592 $ 143,701 $ 362,149 $ 273,534  
Contract with Customer, Liability 0   0   $ 0
Net product revenue | Non-US          
Revenue recognition          
Revenue 108,900 86,900 241,800 168,100  
Emflaza | United States          
Revenue recognition          
Revenue 65,700 56,800 120,300 105,400  
Translarna | Non-US          
Revenue recognition          
Revenue $ 96,500 $ 77,000 $ 211,600 $ 156,200