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Revenue recognition - Net Product Sales (Details)
$ in Thousands
3 Months Ended 9 Months Ended
Sep. 30, 2023
USD ($)
segment
country
Distributor
Sep. 30, 2022
USD ($)
Distributor
segment
country
Sep. 30, 2023
USD ($)
country
Distributor
segment
Sep. 30, 2022
USD ($)
country
segment
Distributor
Dec. 31, 2022
USD ($)
Revenue recognition          
Number of operating segments | segment 1 1 1 1  
Revenue $ 196,576 $ 217,127 $ 630,766 $ 531,389  
Net product revenue | United States          
Revenue recognition          
Number of countries exceeding 10% of net product sales | country 1        
Net product revenue | Geographic concentration risk          
Revenue recognition          
Number of countries exceeding 10% of net product sales | country 1 2 3 2  
Percentage of net product sales threshold 10.00% 10.00% 10.00% 10.00%  
Net product revenue | Geographic concentration risk | United States          
Revenue recognition          
Revenue $ 67,400 $ 54,800 $ 187,700 $ 160,100  
Net product revenue | Geographic concentration risk | Russia          
Revenue recognition          
Revenue   $ 28,300 69,000 $ 57,100  
Net product revenue | Geographic concentration risk | Brazil          
Revenue recognition          
Revenue     $ 52,500    
Net product revenue | Customer concentration risk          
Revenue recognition          
Number of distributors | Distributor 3 2 2 2  
Percentage of net product sales threshold 10.00% 10.00% 10.00% 10.00%  
Net product revenue          
Revenue recognition          
Revenue $ 144,038 $ 134,186 $ 506,187 $ 407,720  
Contract with Customer, Liability 0   0   $ 0
Net product revenue | Non-US          
Revenue recognition          
Revenue 76,600 79,400 318,500 247,600  
Emflaza | United States          
Revenue recognition          
Revenue 67,400 54,800 187,700 160,100  
Translarna | Non-US          
Revenue recognition          
Revenue $ 69,000 $ 76,600 $ 280,600 $ 232,900