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Revenue recognition - Net Product Sales (Details)
$ in Thousands
3 Months Ended
Mar. 31, 2025
USD ($)
segment
country
Distributor
Mar. 31, 2024
USD ($)
segment
Distributor
country
Dec. 31, 2024
USD ($)
Revenue recognition      
Number of operating segments | segment 1 1  
Revenue $ 1,176,096 $ 210,118  
Net product revenue | Geographic concentration risk      
Revenue recognition      
Number of countries exceeding 10% of net product sales | country 2 2  
Percentage of net product sales threshold 10.00% 10.00%  
Net product revenue | Geographic concentration risk | United States      
Revenue recognition      
Revenue $ 47,800 $ 57,500  
Net product revenue | Geographic concentration risk | Non-US      
Revenue recognition      
Revenue 105,600 120,100  
Net product revenue | Geographic concentration risk | Russia      
Revenue recognition      
Revenue $ 38,500 $ 52,600  
Net product revenue | Customer concentration risk      
Revenue recognition      
Number of distributors | Distributor 2 2  
Percentage of net product sales threshold 10.00% 10.00%  
Product      
Revenue recognition      
Revenue $ 153,426 $ 177,604  
Contract with customer, liability 0   $ 0
Emflaza | Net product revenue | Geographic concentration risk | United States      
Revenue recognition      
Revenue 47,800 57,500  
Translarna | Net product revenue | Geographic concentration risk | Non-US      
Revenue recognition      
Revenue $ 86,200 $ 103,600