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MAJOR CUSTOMERS, PARTNERSHIPS AND STRATEGIC ALLIANCES - Pfizer Inc. (Details)
$ in Millions
1 Months Ended 12 Months Ended 70 Months Ended 77 Months Ended
Sep. 30, 2020
USD ($)
Dec. 31, 2017
USD ($)
May 31, 2017
USD ($)
milestone
Dec. 31, 2020
USD ($)
Sep. 30, 2023
USD ($)
milestone
product
Sep. 30, 2023
USD ($)
milestone
Pfizer Inc.            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Agreement termination, term     15 years      
Pfizer Inc. | S B Five Two Five And Other Products            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Revenues under agreement     $ 70.0      
Potential amount to be funded for achievement of specified commercialized and sales milestones     266.5      
Pfizer Inc. | S B Five Two Five And Other Products | Achievement of specified clinical development intellectual property and regulatory milestones            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Development and sales-based milestone payments to be received     208.5      
Pfizer Inc. | S B Five Two Five            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Milestone revenue receivable     220.0      
Pfizer Inc. | Other products            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Milestone revenue receivable     $ 175.0      
Pfizer Inc. | License | Minimum            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   14.00% 14.00%      
Pfizer Inc. | License | Maximum            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   20.00% 20.00%      
Pfizer Inc. | C9ORF72            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Revenues under agreement   $ 5.0   $ 5.0    
Development and sales-based milestone payments to be received $ 5.0          
Collaborative arrangement transaction price   $ 17.0        
Pfizer SB-525            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Revenues under agreement     $ 55.0      
Collaborative arrangement transaction price     134.0      
Research service fees     $ 79.0      
Pfizer SB-525 | S B Five Two Five And Other Products            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Collaborative arrangement, number of milestones achieved | milestone     2     2
Milestone payments received           $ 55.0
Pfizer C9ORF72            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Agreement termination, term   15 years        
Pfizer C9ORF72 | C9ORF72            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Revenues under agreement   $ 12.0        
Milestone payments received   12.0     $ 5.0  
Number of products approved | product         0  
Number of milestones included in transaction price | milestone         0  
Pfizer C9ORF72 | C9ORF72 | Achievement Of Specified Preclinical Development Clinical Development And First Commercial Sale Milestones | Maximum            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Development and sales-based milestone payments to be received   60.0        
Pfizer C9ORF72 | C9ORF72 | Achievement Of Commercial Milestones | Maximum            
Research and Development Arrangement, Contract to Perform for Others [Line Items]            
Development and sales-based milestone payments to be received   $ 90.0