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MAJOR CUSTOMERS, PARTNERSHIPS AND STRATEGIC ALLIANCES - Pfizer Inc. (Details)
$ in Millions
1 Months Ended 12 Months Ended 76 Months Ended 83 Months Ended
Dec. 31, 2017
USD ($)
May 31, 2017
USD ($)
Dec. 31, 2020
USD ($)
Mar. 31, 2024
USD ($)
product
milestone
Mar. 31, 2024
USD ($)
milestone
Pfizer Inc.          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Agreement termination, term   15 years      
Pfizer Inc. | S B Five Two Five And Other Products          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Revenues under agreement   $ 70.0      
Potential amount to be funded for achievement of specified commercialized and sales milestones   266.5      
Pfizer Inc. | S B Five Two Five And Other Products | Achievement of specified clinical development intellectual property and regulatory milestones          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Development and sales-based milestone payments to be received   208.5      
Pfizer Inc. | S B Five Two Five          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Milestone revenue receivable   220.0      
Pfizer Inc. | Other products          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Milestone revenue receivable   $ 175.0      
Pfizer Inc. | License | Minimum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   14.00%      
Pfizer Inc. | License | Maximum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   20.00%      
Pfizer SB-525          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Collaborative arrangement transaction price     $ 134.0    
Pfizer SB-525 | S B Five Two Five And Other Products          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Collaborative arrangement, number of milestones achieved | milestone         2
Milestone payments received         $ 55.0
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Agreement termination, term 15 years        
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Minimum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Percentage of net sales per developed licensed product which will trigger royalties by counterparty 14.00%        
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Maximum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Percentage of net sales per developed licensed product which will trigger royalties by counterparty 20.00%        
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Milestone payments received $ 12.0     $ 5.0  
Collaborative arrangement transaction price 17.0        
Number of products approved | product       0  
Number of milestones included in transaction price | milestone       0  
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72 | Achievement Of Specified Preclinical Development Clinical Development And First Commercial Sale Milestones | Maximum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Development and sales-based milestone payments to be received 60.0        
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72 | Achievement Of Commercial Milestones | Maximum          
Research and Development Arrangement, Contract to Perform for Others [Line Items]          
Development and sales-based milestone payments to be received $ 90.0