XML 51 R36.htm IDEA: XBRL DOCUMENT v3.24.3
MAJOR CUSTOMERS, PARTNERSHIPS AND STRATEGIC ALLIANCES - Pfizer Inc. (Details)
1 Months Ended 3 Months Ended 9 Months Ended 12 Months Ended 37 Months Ended 82 Months Ended 89 Months Ended
Dec. 31, 2017
USD ($)
May 31, 2017
USD ($)
Sep. 30, 2024
USD ($)
Sep. 30, 2023
USD ($)
Sep. 30, 2024
USD ($)
Sep. 30, 2023
USD ($)
Dec. 31, 2020
USD ($)
Dec. 31, 2020
USD ($)
Sep. 30, 2024
USD ($)
milestone
product
Sep. 30, 2024
USD ($)
milestone
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues     $ 49,412,000 $ 9,398,000 $ 50,249,000 $ 174,190,000        
Pfizer Inc.                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Agreement termination, term   15 years                
Pfizer Inc. | S B Five Two Five And Other Products                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Revenues under agreement   $ 70,000,000                
Potential amount to be funded for achievement of specified commercialized and sales milestones   266,500,000                
Pfizer Inc. | S B Five Two Five And Other Products | Achievement of specified clinical development intellectual property and regulatory milestones                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Development and sales-based milestone payments to be received   208,500,000                
Pfizer Inc. | S B Five Two Five                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Milestone revenue receivable   $ 220,000,000                
Pfizer Inc. | License | Minimum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   14.00%                
Pfizer Inc. | License | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty   20.00%                
Pfizer SB-525                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Collaborative arrangement transaction price             $ 134,000,000      
Revenues     0 0 0 0        
Pfizer SB-525 | S B Five Two Five And Other Products                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Collaborative arrangement, number of milestones achieved | milestone                   2
Milestone payments received                   $ 55,000,000
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Agreement termination, term 15 years                  
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Minimum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty 14.00%                  
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | License | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Percentage of net sales per developed licensed product which will trigger royalties by counterparty 20.00%                  
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Milestone payments received $ 12,000,000               $ 5,000,000  
Collaborative arrangement transaction price               $ 17,000,000    
Number of products approved | product                 0  
Number of milestones included in transaction price | milestone                 0  
Revenues     $ 0 $ 0 $ 0 $ 0        
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72 | Achievement Of Specified Preclinical Development Clinical Development And First Commercial Sale Milestones | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Development and sales-based milestone payments to be received 60,000,000                  
Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease | C9ORF72 | Achievement Of Commercial Milestones | Maximum                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                    
Development and sales-based milestone payments to be received $ 90,000,000