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Income Taxes - Components of the Company's Deferred Tax Assets (Liabilities) (Detail) (USD $)
Dec. 31, 2013
Dec. 31, 2012
Deferred income tax assets:    
Federal U.S. net operating loss carryforward $ 36,561,195 $ 35,330,167
State net operating loss carryforward 3,315,514 3,521,722
Research and development credit, net 3,785,612 2,777,899
Orphan drug credit, net 19,883,076 19,039,613
Deferred rent 5,132,458 5,218,002
Deferred revenue 8,216,695 9,379,064
Depreciation 1,438,477 1,247,772
Other 1,438,870 1,575,782
Gross deferred income tax assets 79,771,897 78,090,021
Valuation allowance (79,376,945) (78,090,021)
Net deferred income tax assets 394,952  
Deferred income tax liabilities:    
Other (394,952)  
Gross deferred income tax liabilities (394,952)  
Net deferred income tax asset/(liability)